Title of Study. Bone Health in Boys with Duchenne Muscular Dystrophy (DMD)
Funding Status. Planned PCORI LOI Submission, Cycle 2
Project Focus/Research Question. Bone health in bones with DMD is a significant health issue. Leveraging the CDM, this project will create a computable DMD phenotype and examine outcomes of boys treated with different pharmacologic and non-pharmacologic interventions to promote bone health. Outcomes include fractures and measures of bone density.
Study Design. Pragmatic Clinical Trial